^Ad hoc announcement pursuant to Art. 53 LR

* Aprocitentan, Idorsia's oral, dual endothelin receptor antagonist is

currently under review with health authorities for the treatment of patients

with resistant hypertension.

* Idorsia will pay Janssen a conditional consideration up to a total cap of

CHF 306 million

* Idorsia is initiating activities to determine the best approach to maximize

the value of aprocitentan.

Allschwil, Switzerland - September 6, 2023

Idorsia Ltd (SIX: IDIA) today announced that it has entered into an agreement

with Janssen Biotech Inc., one of the Janssen Pharmaceutical Companies of

Johnson & Johnson, for the return of rights for aprocitentan to Idorsia. In

return, Idorsia is committed to pay up to 306 million Swiss francs, subject to

marketing application approval by the US FDA and Europe's EMA.

Jean-Paul Clozel, CEO of Idorsia, commented:

"I'm happy that we have come to an agreement for the return of aprocitentan to

Idorsia. Aprocitentan has demonstrated significant and clinically meaningful

sustained blood pressure lowering benefits with a good safety profile,

particularly suited to the high-risk patient population with resistant

hypertension. Revolutionizing the use of endothelin receptor antagonism is

something the team at Idorsia knows all about. We will now determine the best

approach to maximizing the value of our exciting new anti-hypertension therapy."

The founding team at Idorsia brought the first oral, dual endothelin receptor

antagonist (ERA) to market, followed by the discovery, development, and launch

of a next generation oral, dual ERA. The team will now evaluate options for

realizing the value which the company has created by successfully developing

aprocitentan, the first anti-hypertensive therapy which works via a new

mechanism of action in 30 years.

About the agreement

Idorsia will reacquire the development and commercialization rights for

aprocitentan from Janssen. In return, Idorsia will pay Janssen a conditional

consideration up to a total cap of CHF 306 million, depending on Idorsia's

revenues, as follows:

* 30% of any consideration received by Idorsia from a potential out-licensing

or divestment of aprocitentan,

* 10% of any consideration received by Idorsia from a potential out-licensing

or the divestment of any other Idorsia product, following the first approval

of aprocitentan, and

* low- to mid-single digit royalties on total group product net sales,

beginning from the quarter after first aprocitentan approval.

Janssen funding obligations to aprocitentan cease at the effective date of the

agreement. Janssen licenses to aprocitentan IP (excluding pulmonary

hypertension) will terminate and Janssen will transfer the brand name and

relating commercial materials to Idorsia. Janssen will retain licenses in the

pulmonary hypertension field.

The agreement also eliminates the revenue-sharing agreement in respect of

ponesimod.

The agreement will be effective following receipt of the clearance relating to

the United States Hart-Scott Rodino Antitrust Improvements Act of 1976.

André C. Muller, Chief Financial Officer, commented:

"If aprocitentan is approved in the US and Europe as we expect, Idorsia would

have an additional product in its portfolio giving the company more strategic

flexibility, and potentially allows Janssen to recoup over time their investment

in aprocitentan."

About the regulatory status of aprocitentan

A new drug application (NDA) for aprocitentan was filed with the US FDA in

December 2022 (Prescription Drug User Fee Act (PDUFA) current date: December

19, 2023), and the market authorisation application (MAA) was submitted to the

EMA at the end of January 2023.

Jean-Paul Clozel, concluded:

"The review process with the US FDA is progressing well, though it is likely to

require an extension to the review period of up to 3 months as the company will

provide additional Risk Evaluation and Mitigation Strategy (REMS) materials to

support a streamlined REMS which is designed specifically for patients taking

aprocitentan."

About aprocitentan in resistant hypertension

Full results from the PRECISION study were published in November 2022 in The

Lancet "A randomized controlled trial of the dual endothelin antagonist

aprocitentan for resistant hypertension

(https://www.thelancet.com/journals/lancet/article/PIIS0140-

6736(22)02034-7/fulltext)". More details and commentary can be found in the

dedicated press release (https://www.idorsia.com/investors/news-and-

events/media-release-details?newsId=2869821) and an investor webcast

(https://www.idorsia.com/investors/news-and-events/Apro-session-AHA-2022)

featuring Prof. Markus Schlaich, an investigator in PRECISION.

Patients with uncontrolled blood pressure are at risk of major cardiovascular

events.(1) These risks are even higher for patients whose blood pressure is

uncontrolled despite treatment with three or more antihypertensives(2), known as

resistant hypertension(3,4). It has been more than 30 years since a new anti-

hypertensive therapy working by a new mechanism has been brought to patients. By

targeting a currently unopposed pathophysiologic pathway, aprocitentan

represents a potential novel, effective, and well-tolerated treatment for

resistant hypertension.

Notes to the editor

The endothelin system in systemic hypertension

Endothelin-1 (ET-1) is a potent vasoconstrictor that also induces neurohormonal

activation, vascular hypertrophy and remodeling, cardiac hypertrophy and

fibrosis, and endothelial dysfunction. In hypertension, both ET(A) and ET(B)

receptors mediate harmful effects of ET-1.(4) As a vasoconstrictor, co-mitogenic

agent, linking pulse pressure and vascular remodeling, and mediator of

aldosterone and catecholamine release, endothelin is a key player in

hypertension and end-organ damage.(5,)(6)

About difficult-to-control (resistant) hypertension

Hypertension (high blood pressure) is one of the most common cardiovascular risk

factors, and its prevalence continues to rise. According to a recent study,

there are more than 1.3 billion people living with hypertension worldwide(6) - a

startling number, which has almost doubled in the past 40 years. Left

uncontrolled, people have a greater risk of life-threatening conditions such as

heart attack, stroke, and chronic kidney disease.(7)

Patients with hypertension can often successfully control their blood pressure

by combining a healthier lifestyle with effective medication. However,

approximately 10% of patients have difficult-to-control hypertension where the

blood pressure remains high despite receiving at least three antihypertensive

medications of different pharmacological classes, including a diuretic, at

optimal doses,(3)(,)(8) (also categorized in hypertension guidelines and the

medical community as having resistant hypertension).

The endothelin pathway has been implicated in the pathogenesis of hypertension,

especially in volume- and salt-dependent forms, which are a common feature in

patients with resistant hypertension. The endothelin pathway has not been

targeted by existing anti-hypertensive therapies until now, thereby leaving this

relevant pathophysiologic pathway unopposed with currently available

medications.(3,9,10) The endothelin system is also activated in patients prone

to developing resistant hypertension, such as Black or African American

patients, patients with obesity or obstructive sleep apnea,(1)(1)(-1)(3) and in

comorbid conditions frequently associated with resistant hypertension such as

diabetes and chronic kidney disease.(1)(4)(-1)(7)

About aprocitentan

Aprocitentan is an investigational, novel, oral, dual endothelin receptor

antagonist (ERA), which potently inhibits the binding of ET-1 to ET(A) and ET(B)

receptors. Aprocitentan has a low potential for drug-drug interaction and a

mechanism of action that is ideally suited for the pathophysiology of resistant

hypertension.

About PRECISION(18,19) (NCT03541174

(https://www.clinicaltrials.gov/ct2/show/NCT03541174))

PRECISION was a multicenter, blinded, randomized, parallel-group, Phase 3 study,

which was performed in hospitals or research centers in Europe, North America,

Asia, and Australia. Patients were eligible for randomization if their sitting

systolic blood pressure was 140 mm Hg or higher despite taking standardized

background therapy consisting of three antihypertensive drugs, including a

diuretic. The study consisted of three sequential parts: Part 1 was the 4-week

double-blind, randomized, and placebo-controlled part, in which 730 patients

were randomized to aprocitentan 12.5 mg (n=243), aprocitentan 25 mg (n=243), or

placebo (n=244) in a 1:1:1 ratio; Part 2 was a 32-week single (patient)-blind

part, in which all patients received aprocitentan 25 mg (n=704); and Part 3 was

a 12-week double-blind, randomized, and placebo-controlled withdrawal part, in

which patients were re-randomized to aprocitentan 25 mg (n=307) or placebo

(n=307) in a 1:1 ratio. The primary and key secondary endpoints were changes in

unattended office systolic blood pressure from baseline to week 4 and from

withdrawal baseline to week 40, respectively. Secondary endpoints included 24-h

ambulatory blood pressure changes.

At baseline, 69.2% of patients were obese or severely obese, 54.1% had diabetes,

22.2% had stage 3-4 chronic kidney disease and 19.6% had congestive heart

failure. 63% of randomized patients were receiving at least 4 anti-hypertensive

therapies at screening.

Key PRECISION findings(19)

The least square mean change in office SBP at 4 weeks was -15.3 mmHg for

aprocitentan 12.5 mg, -15.2 mmHg for 25 mg, and -11.5 mmHg for placebo, for a

difference versus placebo of -3.8 mmHg (p=0.0042) and -3.7 mmHg (p=0.0046),

respectively. Office diastolic blood pressure (DBP) also decreased with both

aprocitentan doses compared to placebo (-3.9 mmHg for the 12.5 mg dose and -4.5

mmHg for the 25 mg dose). Office SBP and DBP were maintained during Part 2 in

patients previously receiving aprocitentan and decreased within the first 2

weeks of Part 2 before stabilizing in those previously receiving placebo. In

Part 3, office SBP after 4 weeks of withdrawal (the key secondary endpoint)

increased significantly with placebo compared to aprocitentan (5.8 mmHg;

p°

Quelle: dpa-AFX